AU - Brunetti-Pierri N FAU - Brunetti-Pierri, Nicola AU - Auricchio A FAU - Auricchio, Alberto AU - Valle D FAU - Valle, David L. AU - Antonarakis S FAU - Antonarakis, Stylianos AU - Ballabio A FAU - Ballabio, Andrea AU - Beaudet A FAU - Beaudet, Arthur L. AU - Mitchell G FAU - Mitchell, Grant A. TI - Gene Therapy of Human Inherited Diseases PT - BOOK SECTION DP - 2019 BTI - The Online Metabolic and Molecular Bases of Inherited Disease DA - 2019 Y2 - 2024/11/10 UR - ommbid.mhmedical.com/content.aspx?aid=1181401143