@inbook{1181401143, author={Nicola Brunetti-Pierri and Alberto Auricchio}, editor={Valle, David L. and Antonarakis, Stylianos and Ballabio, Andrea and Beaudet, Arthur L. and Mitchell, Grant A.}, title={Gene Therapy of Human Inherited Diseases}, booktitle={The Online Metabolic and Molecular Bases of Inherited Disease}, publisher={McGraw-Hill Education}, address={New York, NY}, year={2019}, url={ommbid.mhmedical.com/content.aspx?aid=1181401143} }